Edited by jsam at 2024-4-28 22:30
Title: Challenges and opportunities in spinal muscular atrophy therapeutics
Authors: Crystal J J Yeo , Eduardo F Tizzano , Basil T Darras
Journal: Lancet Neurology. 2024 Feb;23(2):205-218
DOI: 10.1016/S1474-4422(23)00419-2
PMID: 38267192
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