[Ovid]
Long-term Follow-up of Cipaglucosidase Alfa/Miglustat in Ambulatory Patients with Pompe Disease: An Open-label Phase I/II Study (ATB200-02) (S48.007)
Authors£ºTahseen Mozaffar; Benedikt Schoser; Priya Kishnani; Drago Bratkovic; Paula R. Clemens; Ozlem Goker-Alpan; Xue Ming; Mark Roberts; Kumaraswamy Sivakumar; Ans Van Der Ploeg; Mitchell Goldman; Jacquelyn Wright; Fred Holdbrook; Vipul Jain; Sheela Sitaraman; Yasmine Wasfi; Barry Byrne